Cargando…
Neonatal umbilical cord blood transplantation halts skeletal disease progression in the murine model of MPS-I
Umbilical cord blood (UCB) is a promising source of stem cells to use in early haematopoietic stem cell transplantation (HSCT) approaches for several genetic diseases that can be diagnosed at birth. Mucopolysaccharidosis type I (MPS-I) is a progressive multi-system disorder caused by deficiency of l...
Autores principales: | Azario, Isabella, Pievani, Alice, Del Priore, Federica, Antolini, Laura, Santi, Ludovica, Corsi, Alessandro, Cardinale, Lucia, Sawamoto, Kazuki, Kubaski, Francyne, Gentner, Bernhard, Bernardo, Maria Ester, Valsecchi, Maria Grazia, Riminucci, Mara, Tomatsu, Shunji, Aiuti, Alessandro, Biondi, Andrea, Serafini, Marta |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Nature Publishing Group UK
2017
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5573317/ https://www.ncbi.nlm.nih.gov/pubmed/28842642 http://dx.doi.org/10.1038/s41598-017-09958-9 |
Ejemplares similares
-
Neonatal cellular and gene therapies for mucopolysaccharidoses: the earlier the better?
por: Tomatsu, Shunji, et al.
Publicado: (2015) -
Acute myeloid leukemia shapes the bone marrow stromal niche in vivo
por: Pievani, Alice, et al.
Publicado: (2020) -
Bone mineral density in mucopolysaccharidosis IVB
por: Kubaski, Francyne, et al.
Publicado: (2016) -
Neonatal Screening for MPS Disorders in Latin America: A Survey of Pilot Initiatives
por: Kubaski, Francyne, et al.
Publicado: (2020) -
MPSI Manifestations and Treatment Outcome: Skeletal Focus
por: De Ponti, Giada, et al.
Publicado: (2022)