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Treatment With Tafamidis Slows Disease Progression in Early-Stage Transthyretin Cardiomyopathy
BACKGROUND: Transthyretin cardiomyopathy (TTR-CM) is a progressive, fatal disease caused by the accumulation of misfolded transthyretin (TTR) amyloid fibrils in the heart. Tafamidis is a kinetic stabilizer of TTR that inhibits misfolding and amyloid formation. METHODS: In this post hoc analysis, dat...
Autores principales: | Sultan, Marla B, Gundapaneni, Balarama, Schumacher, Jennifer, Schwartz, Jeffrey H |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
SAGE Publications
2017
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5606341/ https://www.ncbi.nlm.nih.gov/pubmed/28951660 http://dx.doi.org/10.1177/1179546817730322 |
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