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Treatment With Tafamidis Slows Disease Progression in Early-Stage Transthyretin Cardiomyopathy

BACKGROUND: Transthyretin cardiomyopathy (TTR-CM) is a progressive, fatal disease caused by the accumulation of misfolded transthyretin (TTR) amyloid fibrils in the heart. Tafamidis is a kinetic stabilizer of TTR that inhibits misfolding and amyloid formation. METHODS: In this post hoc analysis, dat...

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Detalles Bibliográficos
Autores principales: Sultan, Marla B, Gundapaneni, Balarama, Schumacher, Jennifer, Schwartz, Jeffrey H
Formato: Online Artículo Texto
Lenguaje:English
Publicado: SAGE Publications 2017
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5606341/
https://www.ncbi.nlm.nih.gov/pubmed/28951660
http://dx.doi.org/10.1177/1179546817730322

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