Efficacy of Idebenone to Preserve Respiratory Function above Clinically Meaningful Thresholds for Forced Vital Capacity (FVC) in Patients with Duchenne Muscular Dystrophy

BACKGROUND: Patients with DMD experience progressive restrictive respiratory disease and eventual respiratory failure. Standard of care guidelines command changes in disease management when forced vital capacity percent of predicted (FVC% p) falls below clinically relevant thresholds. The Phase 3 DE...

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Detalles Bibliográficos
Autores principales: Mayer, Oscar H., Leinonen, Mika, Rummey, Christian, Meier, Thomas, Buyse, Gunnar M.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: IOS Press 2017
Materias:
Research Report
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5611828/
https://www.ncbi.nlm.nih.gov/pubmed/28869486
http://dx.doi.org/10.3233/JND-170245

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