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Regulatory and Scientific Advancements in Gene Therapy: State-of-the-Art of Clinical Applications and of the Supporting European Regulatory Framework

Advanced therapy medicinal products (ATMPs) have a massive potential to address existing unmet medical needs. Specifically, gene therapy medicinal products (GTMPs) may potentially provide cure for several genetic diseases. In Europe, the ATMP regulation was fully implemented in 2009 and, at this poi...

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Detalles Bibliográficos
Autores principales:	Carvalho, Marta, Sepodes, Bruno, Martins, Ana Paula
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Frontiers Media S.A. 2017
Materias:	Medicine
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5662580/ https://www.ncbi.nlm.nih.gov/pubmed/29124055 http://dx.doi.org/10.3389/fmed.2017.00182

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