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The humanistic burden of Pompe disease: are there still unmet needs? A systematic review

BACKGROUND: Humanistic burden considers the impact of an illness on a patient’s health-related quality of life (HRQoL), activities of daily living (ADL), caregiver health, and caregiver QoL. Humanistic burden also considers treatment satisfaction and adherence to treatment regimens. Pompe disease is...

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Detalles Bibliográficos
Autores principales:	Schoser, Benedikt, Bilder, Deborah A., Dimmock, David, Gupta, Digant, James, Emma S., Prasad, Suyash
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2017
Materias:	Research Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5700516/ https://www.ncbi.nlm.nih.gov/pubmed/29166883 http://dx.doi.org/10.1186/s12883-017-0983-2

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