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Patients with rare diseases: from therapeutic orphans to pioneers of personalized treatments
Common diseases, such as cancer, diabetes mellitus, or Alzheimer's disease, affect a large segment of the population, which justifies the enormous financial allocations for translational and clinical research. In contrast, the ~5,000 known rare disorders affect only very few patients each, even...
Autores principales: | Klein, Christoph, Gahl, William A |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
John Wiley and Sons Inc.
2017
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5760852/ https://www.ncbi.nlm.nih.gov/pubmed/29180354 http://dx.doi.org/10.15252/emmm.201708365 |
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