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Genetic Correction of Sickle Cell Anemia and β-Thalassemia: Progress and New Perspective

Gene therapy for β-globinopathies, particularly β-thalassemia and sickle cell anemia, holds promise for the future as a definitive corrective approach for these common and debilitating disorders. Correction of the β-globinopathies using lentivirus vectors carrying the β- or γ-globin genes and elemen...

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Detalles Bibliográficos
Autores principales:	Perumbeti, Ajay, Malik, Punam
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	TheScientificWorldJOURNAL 2010
Materias:	Review Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5763711/ https://www.ncbi.nlm.nih.gov/pubmed/20419277 http://dx.doi.org/10.1100/tsw.2010.67

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