Characteristics of drugs for ultra-rare diseases versus drugs for other rare diseases in HTA submissions made to the CADTH CDR

BACKGROUND: It has been suggested that ultra-rare diseases should be recognized as distinct from more prevalent rare diseases, but how drugs developed to treat ultra-rare diseases (DURDs) might be distinguished from drugs for ‘other’ rare diseases (DORDs) is not clear. We compared the characteristic...

Descripción completa

Detalles Bibliográficos
Autores principales: Richter, Trevor, Janoudi, Ghayath, Amegatse, William, Nester-Parr, Sandra
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BioMed Central 2018
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5793441/
https://www.ncbi.nlm.nih.gov/pubmed/29386040
http://dx.doi.org/10.1186/s13023-018-0762-1

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5793441/
https://www.ncbi.nlm.nih.gov/pubmed/29386040
http://dx.doi.org/10.1186/s13023-018-0762-1

Ejemplares similares