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The potential of antisense oligonucleotide therapies for inherited childhood lung diseases
Antisense oligonucleotides are an emerging therapeutic option to treat diseases with known genetic origin. In the age of personalised medicines, antisense oligonucleotides can sometimes be designed to target and bypass or overcome a patient’s genetic mutation, in particular those lesions that compro...
Autores principales: | Martinovich, Kelly M., Shaw, Nicole C., Kicic, Anthony, Schultz, André, Fletcher, Sue, Wilton, Steve D., Stick, Stephen M. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Springer Berlin Heidelberg
2018
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5801198/ https://www.ncbi.nlm.nih.gov/pubmed/29411170 http://dx.doi.org/10.1186/s40348-018-0081-6 |
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