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Taliglucerase alfa: safety and efficacy across 6 clinical studies in adults and children with Gaucher disease

Taliglucerase alfa is an enzyme replacement therapy (ERT) approved for treatment of adult and paediatric patients with Type 1 Gaucher disease (GD) in several countries and the first plant cell–expressed recombinant therapeutic protein approved by the US Food and Drug Administration for humans. Here,...

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Detalles Bibliográficos
Autores principales:	Zimran, Ari, Wajnrajch, Michael, Hernandez, Betina, Pastores, Gregory M.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2018
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5824466/ https://www.ncbi.nlm.nih.gov/pubmed/29471850 http://dx.doi.org/10.1186/s13023-018-0776-8

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