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Post‐transplant adaptive function in childhood cerebral adrenoleukodystrophy

OBJECTIVE: Hematopoietic stem cell transplantation (HSCT) is the only treatment known to slow or halt inflammatory demyelination among boys with the cerebral form of X‐linked adrenoleukodystrophy (cALD), a devastating childhood condition affecting the central nervous system. HSCT can lead to a range...

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Detalles Bibliográficos
Autores principales:	Pierpont, Elizabeth I., McCoy, Erin, King, Kelly E., Ziegler, Rich S., Shanley, Ryan, Nascene, David, Raymond, Gerald V., Phelan, Rachel, Lund, Troy C., Orchard, Paul J., Miller, Weston P.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	John Wiley and Sons Inc. 2018
Materias:	Research Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5846389/ https://www.ncbi.nlm.nih.gov/pubmed/29560371 http://dx.doi.org/10.1002/acn3.526

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