Placebo‐controlled crossover assessment of mecasermin for the treatment of Rett syndrome

OBJECTIVE: To measure the efficacy of mecasermin (recombinant human insulin‐like growth factor 1, rhIGF‐1), for treating symptoms of Rett syndrome (RTT) in a pediatric population using a double‐blind crossover study design. METHODS: Thirty girls with classic RTT in postregression stage were randomly...

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Detalles Bibliográficos
Autores principales: O'Leary, Heather M., Kaufmann, Walter E., Barnes, Katherine V., Rakesh, Kshitiz, Kapur, Kush, Tarquinio, Daniel C., Cantwell, Nicole G., Roche, Katherine J., Rose, Suzanne A., Walco, Alexandra C., Bruck, Natalie M., Bazin, Grace A., Holm, Ingrid A., Alexander, Mark E., Swanson, Lindsay C., Baczewski, Lauren M., Mayor Torres, Juan M., Nelson, Charles A., Sahin, Mustafa
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2018
Materias:
Research Articles
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5846450/
https://www.ncbi.nlm.nih.gov/pubmed/29560377
http://dx.doi.org/10.1002/acn3.533

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5846450/
https://www.ncbi.nlm.nih.gov/pubmed/29560377
http://dx.doi.org/10.1002/acn3.533

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