Cargando…
Lupus community panel proposals for optimising clinical trials: 2018
Formidable impediments stand in the way of treatment development for lupus. These include the unwieldy size of current trials, international competition for scarce patients, complex outcome measures and a poor understanding of these outcomes in the world at large. The heterogeneity of the disease it...
Autores principales: | , , , , , , , , , , , , , , , , |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
BMJ Publishing Group
2018
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5894527/ https://www.ncbi.nlm.nih.gov/pubmed/29657738 http://dx.doi.org/10.1136/lupus-2018-000258 |
_version_ | 1783313506476490752 |
---|---|
author | Merrill, Joan T Manzi, Susan Aranow, Cynthia Askenase, Anca Bruce, Ian Chakravarty, Eliza Chong, Ben Costenbader, Karen Dall’Era, Maria Ginzler, Ellen Hanrahan, Leslie Kalunian, Ken Merola, Joseph Raymond, Sandra Rovin, Brad Saxena, Amit Werth, Victoria P |
author_facet | Merrill, Joan T Manzi, Susan Aranow, Cynthia Askenase, Anca Bruce, Ian Chakravarty, Eliza Chong, Ben Costenbader, Karen Dall’Era, Maria Ginzler, Ellen Hanrahan, Leslie Kalunian, Ken Merola, Joseph Raymond, Sandra Rovin, Brad Saxena, Amit Werth, Victoria P |
author_sort | Merrill, Joan T |
collection | PubMed |
description | Formidable impediments stand in the way of treatment development for lupus. These include the unwieldy size of current trials, international competition for scarce patients, complex outcome measures and a poor understanding of these outcomes in the world at large. The heterogeneity of the disease itself coupled to superimposition of variegated background polypharmacy has created enough immunological noise to virtually ensure the failure of lupus treatment trials, leaving an understandable suspicion that at least some of the results in testing failed drugs over the years may not have been negative, but merely uninterpretable. The authors have consulted with many clinical trial investigators, biopharmaceutical developers and stakeholders from government and voluntary sectors. This paper examines the available evidence that supports workable trial designs and proposes approaches to improve the odds of completing interpretable treatment development programs for lupus. |
format | Online Article Text |
id | pubmed-5894527 |
institution | National Center for Biotechnology Information |
language | English |
publishDate | 2018 |
publisher | BMJ Publishing Group |
record_format | MEDLINE/PubMed |
spelling | pubmed-58945272018-04-13 Lupus community panel proposals for optimising clinical trials: 2018 Merrill, Joan T Manzi, Susan Aranow, Cynthia Askenase, Anca Bruce, Ian Chakravarty, Eliza Chong, Ben Costenbader, Karen Dall’Era, Maria Ginzler, Ellen Hanrahan, Leslie Kalunian, Ken Merola, Joseph Raymond, Sandra Rovin, Brad Saxena, Amit Werth, Victoria P Lupus Sci Med Review Formidable impediments stand in the way of treatment development for lupus. These include the unwieldy size of current trials, international competition for scarce patients, complex outcome measures and a poor understanding of these outcomes in the world at large. The heterogeneity of the disease itself coupled to superimposition of variegated background polypharmacy has created enough immunological noise to virtually ensure the failure of lupus treatment trials, leaving an understandable suspicion that at least some of the results in testing failed drugs over the years may not have been negative, but merely uninterpretable. The authors have consulted with many clinical trial investigators, biopharmaceutical developers and stakeholders from government and voluntary sectors. This paper examines the available evidence that supports workable trial designs and proposes approaches to improve the odds of completing interpretable treatment development programs for lupus. BMJ Publishing Group 2018-03-23 /pmc/articles/PMC5894527/ /pubmed/29657738 http://dx.doi.org/10.1136/lupus-2018-000258 Text en © Article author(s) (or their employer(s) unless otherwise stated in the text of the article) 2018. All rights reserved. No commercial use is permitted unless otherwise expressly granted. This is an Open Access article distributed in accordance with the Creative Commons Attribution Non Commercial (CC BY-NC 4.0) license, which permits others to distribute, remix, adapt, build upon this work non-commercially, and license their derivative works on different terms, provided the original work is properly cited and the use is non-commercial. See: http://creativecommons.org/licenses/by-nc/4.0/ |
spellingShingle | Review Merrill, Joan T Manzi, Susan Aranow, Cynthia Askenase, Anca Bruce, Ian Chakravarty, Eliza Chong, Ben Costenbader, Karen Dall’Era, Maria Ginzler, Ellen Hanrahan, Leslie Kalunian, Ken Merola, Joseph Raymond, Sandra Rovin, Brad Saxena, Amit Werth, Victoria P Lupus community panel proposals for optimising clinical trials: 2018 |
title | Lupus community panel proposals for optimising clinical trials: 2018 |
title_full | Lupus community panel proposals for optimising clinical trials: 2018 |
title_fullStr | Lupus community panel proposals for optimising clinical trials: 2018 |
title_full_unstemmed | Lupus community panel proposals for optimising clinical trials: 2018 |
title_short | Lupus community panel proposals for optimising clinical trials: 2018 |
title_sort | lupus community panel proposals for optimising clinical trials: 2018 |
topic | Review |
url | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5894527/ https://www.ncbi.nlm.nih.gov/pubmed/29657738 http://dx.doi.org/10.1136/lupus-2018-000258 |
work_keys_str_mv | AT merrilljoant lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT manzisusan lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT aranowcynthia lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT askenaseanca lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT bruceian lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT chakravartyeliza lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT chongben lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT costenbaderkaren lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT dalleramaria lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT ginzlerellen lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT hanrahanleslie lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT kalunianken lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT merolajoseph lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT raymondsandra lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT rovinbrad lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT saxenaamit lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 AT werthvictoriap lupuscommunitypanelproposalsforoptimisingclinicaltrials2018 |