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Pharmacology of Recombinant Adeno-associated Virus Production

Recombinant adeno-associated viral (rAAV) vectors have been used in more than 150 clinical trials with a good safety profile and significant clinical benefit in many genetic diseases. In addition, due to their ability to infect non-dividing and dividing cells and to serve as efficient substrate for...

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Detalles Bibliográficos
Autores principales:	Penaud-Budloo, Magalie, François, Achille, Clément, Nathalie, Ayuso, Eduard
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	American Society of Gene & Cell Therapy 2018
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5908265/ https://www.ncbi.nlm.nih.gov/pubmed/29687035 http://dx.doi.org/10.1016/j.omtm.2018.01.002

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