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Emerging therapies for hemophilia: controversies and unanswered questions

Several new therapies for hemophilia have emerged in recent years. These strategies range from extended half-life factor replacement products and non-factor options with improved pharmacokinetic profiles to gene therapy aiming for phenotypic cure. While these products have the potential to change he...

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Detalles Bibliográficos
Autores principales:	Arruda, Valder R., Doshi, Bhavya S., Samelson-Jones, Benjamin J.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	F1000 Research Limited 2018
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5931262/ https://www.ncbi.nlm.nih.gov/pubmed/29770199 http://dx.doi.org/10.12688/f1000research.12491.1

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