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The Horizon of a Therapy for Rare Genetic Diseases: A “Druggable” Future for Fibrodysplasia Ossificans Progressiva
Fibrodysplasia ossificans progressiva (FOP) is a rare genetic condition characterized by progressive extra-skeletal ossification leading to cumulative and severe disability. FOP has an extremely variable and episodic course and can be induced by trauma, infections, iatrogenic harms, immunization or...
Autores principales: | Cappato, Serena, Giacopelli, Francesca, Ravazzolo, Roberto, Bocciardi, Renata |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2018
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5979309/ https://www.ncbi.nlm.nih.gov/pubmed/29587443 http://dx.doi.org/10.3390/ijms19040989 |
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