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MicroRNA-206 Downregulation Improves Therapeutic Gene Expression and Motor Function in mdx Mice
Duchenne muscular dystrophy (DMD) is a severe muscle-wasting disorder caused by a mutation in the dystrophin gene. Numerous gene therapies have been developed to replace or repair the defective dystrophin gene; however, these treatments cannot restore the full-length protein or completely resolve dy...
| Autores principales: | , , , , , , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
American Society of Gene & Cell Therapy
2018
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| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6011022/ https://www.ncbi.nlm.nih.gov/pubmed/30195767 http://dx.doi.org/10.1016/j.omtn.2018.05.011 |