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Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy
| Autores principales: | , , , , , , , , , , , , , , , , , , , , , , , , , , , , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
Nature Publishing Group UK
2018
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| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6039388/ https://www.ncbi.nlm.nih.gov/pubmed/29379168 http://dx.doi.org/10.1038/s41409-017-0085-1 |
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| author | Calbi, Valeria Fumagalli, Francesca Consiglieri, Giulia Penati, Rachele Acquati, Serena Redaelli, Daniela Attanasio, Vanessa Marcella, Facchini Cicalese, Maria Pia Migliavacca, Maddalena Barzaghi, Federica Ferrua, Francesca Assanelli, Andrea Silvani, Paolo Zoccolillo, Matteo Chidini, Giovanna Chiesa, Robert Arora, Ruchi Ciotti, Francesca Sarzana, Marina Antonioli, Gigliola Baldoli, Cristina Morena, Francesco Martino, Sabata Ardissino, Gian Luigi Sora, Maria Grazia Natali Naldini, Luigi Ciceri, Fabio Aiuti, Alessandro Bernardo, Maria Ester |
| author_facet | Calbi, Valeria Fumagalli, Francesca Consiglieri, Giulia Penati, Rachele Acquati, Serena Redaelli, Daniela Attanasio, Vanessa Marcella, Facchini Cicalese, Maria Pia Migliavacca, Maddalena Barzaghi, Federica Ferrua, Francesca Assanelli, Andrea Silvani, Paolo Zoccolillo, Matteo Chidini, Giovanna Chiesa, Robert Arora, Ruchi Ciotti, Francesca Sarzana, Marina Antonioli, Gigliola Baldoli, Cristina Morena, Francesco Martino, Sabata Ardissino, Gian Luigi Sora, Maria Grazia Natali Naldini, Luigi Ciceri, Fabio Aiuti, Alessandro Bernardo, Maria Ester |
| author_sort | Calbi, Valeria |
| collection | PubMed |
| description | |
| format | Online Article Text |
| id | pubmed-6039388 |
| institution | National Center for Biotechnology Information |
| language | English |
| publishDate | 2018 |
| publisher | Nature Publishing Group UK |
| record_format | MEDLINE/PubMed |
| spelling | pubmed-60393882018-07-12 Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy Calbi, Valeria Fumagalli, Francesca Consiglieri, Giulia Penati, Rachele Acquati, Serena Redaelli, Daniela Attanasio, Vanessa Marcella, Facchini Cicalese, Maria Pia Migliavacca, Maddalena Barzaghi, Federica Ferrua, Francesca Assanelli, Andrea Silvani, Paolo Zoccolillo, Matteo Chidini, Giovanna Chiesa, Robert Arora, Ruchi Ciotti, Francesca Sarzana, Marina Antonioli, Gigliola Baldoli, Cristina Morena, Francesco Martino, Sabata Ardissino, Gian Luigi Sora, Maria Grazia Natali Naldini, Luigi Ciceri, Fabio Aiuti, Alessandro Bernardo, Maria Ester Bone Marrow Transplant Correspondence Nature Publishing Group UK 2018-01-29 2018 /pmc/articles/PMC6039388/ /pubmed/29379168 http://dx.doi.org/10.1038/s41409-017-0085-1 Text en © The Author(s) 2018 Open Access This article is licensed under a Creative Commons Attribution 4.0 International License, which permits use, sharing, adaptation, distribution and reproduction in any medium or format, as long as you give appropriate credit to the original author(s) and the source, provide a link to the Creative Commons license, and indicate if changes were made. The images or other third party material in this article are included in the article’s Creative Commons license, unless indicated otherwise in a credit line to the material. If material is not included in the article’s Creative Commons license and your intended use is not permitted by statutory regulation or exceeds the permitted use, you will need to obtain permission directly from the copyright holder. To view a copy of this license, visit http://creativecommons.org/licenses/by/4.0/. |
| spellingShingle | Correspondence Calbi, Valeria Fumagalli, Francesca Consiglieri, Giulia Penati, Rachele Acquati, Serena Redaelli, Daniela Attanasio, Vanessa Marcella, Facchini Cicalese, Maria Pia Migliavacca, Maddalena Barzaghi, Federica Ferrua, Francesca Assanelli, Andrea Silvani, Paolo Zoccolillo, Matteo Chidini, Giovanna Chiesa, Robert Arora, Ruchi Ciotti, Francesca Sarzana, Marina Antonioli, Gigliola Baldoli, Cristina Morena, Francesco Martino, Sabata Ardissino, Gian Luigi Sora, Maria Grazia Natali Naldini, Luigi Ciceri, Fabio Aiuti, Alessandro Bernardo, Maria Ester Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy |
| title | Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy |
| title_full | Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy |
| title_fullStr | Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy |
| title_full_unstemmed | Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy |
| title_short | Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy |
| title_sort | use of defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy |
| topic | Correspondence |
| url | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6039388/ https://www.ncbi.nlm.nih.gov/pubmed/29379168 http://dx.doi.org/10.1038/s41409-017-0085-1 |
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