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Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy

Detalles Bibliográficos
Autores principales:	Calbi, Valeria, Fumagalli, Francesca, Consiglieri, Giulia, Penati, Rachele, Acquati, Serena, Redaelli, Daniela, Attanasio, Vanessa, Marcella, Facchini, Cicalese, Maria Pia, Migliavacca, Maddalena, Barzaghi, Federica, Ferrua, Francesca, Assanelli, Andrea, Silvani, Paolo, Zoccolillo, Matteo, Chidini, Giovanna, Chiesa, Robert, Arora, Ruchi, Ciotti, Francesca, Sarzana, Marina, Antonioli, Gigliola, Baldoli, Cristina, Morena, Francesco, Martino, Sabata, Ardissino, Gian Luigi, Sora, Maria Grazia Natali, Naldini, Luigi, Ciceri, Fabio, Aiuti, Alessandro, Bernardo, Maria Ester
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Nature Publishing Group UK 2018
Materias:	Correspondence
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6039388/ https://www.ncbi.nlm.nih.gov/pubmed/29379168 http://dx.doi.org/10.1038/s41409-017-0085-1

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