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Health status decline in α-1 antitrypsin deficiency: a feasible outcome for disease modifying therapies?

BACKGROUND: Trials of disease modifying therapies in Chronic Obstructive Pulmonary Disease (COPD) provide challenges for detecting physiological and patient centred outcomes. The purpose of the current study was to monitor decline in health status in Alpha-1 antitrypsin deficiency (AATD) and determi...

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Detalles Bibliográficos
Autores principales:	Stockley, Robert A., Edgar, Ross G., Starkey, Sian, Turner, Alice M.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2018
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6053712/ https://www.ncbi.nlm.nih.gov/pubmed/30029692 http://dx.doi.org/10.1186/s12931-018-0844-6

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