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A Promising Small Molecule for Vanishing White Matter Disease

Investigators from Calico Life Sciences LLC and AbbVie report the effects of a novel drug targeting the genetic basis of Vanishing White Matter Disease (VWMD).

Detalles Bibliográficos
Autores principales:	Mithal, Divakar S., Rubin, Jennifer P.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Pediatric Neurology Briefs Publishers 2018
Materias:	Degenerative Diseases
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6115330/ https://www.ncbi.nlm.nih.gov/pubmed/30174381 http://dx.doi.org/10.15844/pedneurbriefs-32-5

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