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Validation of an Immunoassay for Anti-thymidine Phosphorylase Antibodies in Patients with MNGIE Treated with Enzyme Replacement Therapy
Erythrocyte encapsulated thymidine phosphorylase is recombinant Escherichia coli thymidine phosphorylase encapsulated within human autologous erythrocytes and is under development as an enzyme replacement therapy for the ultra-rare inherited metabolic disorder mitochondrial neurogastrointestinal enc...
Autores principales: | Levene, Michelle, Pacitti, Dario, Gasson, Charlotte, Hall, Jamie, Sellos-Moura, Marcia, Bax, Bridget E. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
American Society of Gene & Cell Therapy
2018
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6170929/ https://www.ncbi.nlm.nih.gov/pubmed/30294618 http://dx.doi.org/10.1016/j.omtm.2018.08.007 |
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