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Natural History of Vanishing White Matter

OBJECTIVE: To comprehensively describe the natural history of vanishing white matter (VWM), aiming at improving counseling of patients/families and providing natural history data for future therapeutic trials. METHODS: We performed a longitudinal multicenter study among 296 genetically confirmed VWM...

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Detalles Bibliográficos
Autores principales:	Hamilton, Eline M. C., van der Lei, Hannemieke D. W., Vermeulen, Gerre, Gerver, Jan A. M., Lourenço, Charles M., Naidu, Sakkubai, Mierzewska, Hanna, Gemke, Reinoud J. B. J., de Vet, Henrica C. W., Uitdehaag, Bernard M. J., Lissenberg‐Witte, Birgit I., Research Group, VWM, van der Knaap, Marjo S.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	John Wiley and Sons Inc. 2018
Materias:	Research Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6175238/ https://www.ncbi.nlm.nih.gov/pubmed/30014503 http://dx.doi.org/10.1002/ana.25287

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