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Randomized trial of l-serine in patients with hereditary sensory and autonomic neuropathy type 1

OBJECTIVE: To evaluate the safety and efficacy of l-serine in humans with hereditary sensory autonomic neuropathy type I (HSAN1). METHODS: In this randomized, placebo-controlled, parallel-group trial with open-label extension, patients aged 18–70 years with symptomatic HSAN1 were randomized to l-ser...

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Detalles Bibliográficos
Autores principales:	Fridman, Vera, Suriyanarayanan, Saranya, Novak, Peter, David, William, Macklin, Eric A., McKenna-Yasek, Diane, Walsh, Kailey, Aziz-Bose, Razina, Oaklander, Anne Louise, Brown, Robert, Hornemann, Thorsten, Eichler, Florian
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Lippincott Williams & Wilkins 2019
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6345118/ https://www.ncbi.nlm.nih.gov/pubmed/30626650 http://dx.doi.org/10.1212/WNL.0000000000006811

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