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CRISPR to the Rescue: Advances in Gene Editing for the FMR1 Gene
Gene-editing using Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) is promising as a potential therapeutic strategy for many genetic disorders. CRISPR-based therapies are already being assessed in clinical trials, and evaluation of this technology in Fragile X syndrome has been pe...
Autores principales: | Yrigollen, Carolyn M., Davidson, Beverly L. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2019
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6357057/ https://www.ncbi.nlm.nih.gov/pubmed/30669625 http://dx.doi.org/10.3390/brainsci9010017 |
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