The effect of enzyme replacement therapy on clinical outcomes in male patients with Fabry disease: A systematic literature review by a European panel of experts

BACKGROUND: Enzyme replacement therapy (ERT) with recombinant human α-galactosidase has been available for the treatment of Fabry disease since 2001 in Europe and 2003 in the USA. Treatment outcomes with ERT are dependent on baseline patient characteristics, and published data are derived from heter...

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Detalles Bibliográficos
Autores principales: Germain, Dominique P., Elliott, Perry M., Falissard, Bruno, Fomin, Victor V., Hilz, Max J., Jovanovic, Ana, Kantola, Ilkka, Linhart, Aleš, Mignani, Renzo, Namdar, Mehdi, Nowak, Albina, Oliveira, João-Paulo, Pieroni, Maurizio, Viana-Baptista, Miguel, Wanner, Christoph, Spada, Marco
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Elsevier 2019
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6365982/
https://www.ncbi.nlm.nih.gov/pubmed/30775256
http://dx.doi.org/10.1016/j.ymgmr.2019.100454

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