The patient’s view on rare disease trial design – a qualitative study

BACKGROUND: Clinical trials in rare diseases are more challenging than trials in frequent diseases. Small numbers of eligible trial participants, often complicated by heterogeneity among rare disease patients, hamper the design and conduct of a ‘classical’ Randomized Controlled Trial. Therefore, nov...

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Detalles Bibliográficos
Autores principales: Gaasterland, C. M. W., van der Weide, M. C. Jansen –, du Prie – Olthof, M. J., Donk, M., Kaatee, M. M., Kaczmarek, R., Lavery, C., Leeson-Beevers, K., O’Neill, N., Timmis, O., van Nederveen, V., Vroom, E., van der Lee, J. H.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BioMed Central 2019
Materias:
Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6367834/
https://www.ncbi.nlm.nih.gov/pubmed/30732630
http://dx.doi.org/10.1186/s13023-019-1002-z

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