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The Application of Adeno-Associated Viral Vector Gene Therapy to the Treatment of Fragile X Syndrome
Viral vector-mediated gene therapy has grown by leaps and bounds over the past several years. Although the reasons for this progress are varied, a deeper understanding of the basic biology of the viruses, the identification of new and improved versions of viral vectors, and simply the vast experienc...
Autores principales: | Hampson, David R., Hooper, Alexander W. M., Niibori, Yosuke |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2019
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6406794/ https://www.ncbi.nlm.nih.gov/pubmed/30717399 http://dx.doi.org/10.3390/brainsci9020032 |
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