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Long-term Evaluation of AAV-CRISPR Genome Editing for Duchenne Muscular Dystrophy
Autores principales: | Nelson, Christopher E., Wu, Yaoying, Gemberling, Matthew P., Oliver, Matthew L., Waller, Matthew A., Bohning, Joel D., Robinson-Hamm, Jacqueline N., Bulaklak, Karen, Castellanos Rivera, Ruth M., Collier, Joel H., Asokan, Aravind, Gersbach, Charles A. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
2019
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6455975/ https://www.ncbi.nlm.nih.gov/pubmed/30778238 http://dx.doi.org/10.1038/s41591-019-0344-3 |
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