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Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction

Detalles Bibliográficos
Autores principales: Han, Sang-oh, Ronzitti, Giuseppe, Arnson, Benjamin, Leborgne, Christian, Li, Songtao, Mingozzi, Federico, Koeberl, Dwight
Formato: Online Artículo Texto
Lenguaje:English
Publicado: American Society of Gene & Cell Therapy 2019
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6500922/
https://www.ncbi.nlm.nih.gov/pubmed/31073535
http://dx.doi.org/10.1016/j.omtm.2019.04.005
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author Han, Sang-oh
Ronzitti, Giuseppe
Arnson, Benjamin
Leborgne, Christian
Li, Songtao
Mingozzi, Federico
Koeberl, Dwight
author_facet Han, Sang-oh
Ronzitti, Giuseppe
Arnson, Benjamin
Leborgne, Christian
Li, Songtao
Mingozzi, Federico
Koeberl, Dwight
author_sort Han, Sang-oh
collection PubMed
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spelling pubmed-65009222019-05-09 Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction Han, Sang-oh Ronzitti, Giuseppe Arnson, Benjamin Leborgne, Christian Li, Songtao Mingozzi, Federico Koeberl, Dwight Mol Ther Methods Clin Dev Article American Society of Gene & Cell Therapy 2019-05-01 /pmc/articles/PMC6500922/ /pubmed/31073535 http://dx.doi.org/10.1016/j.omtm.2019.04.005 Text en © 2017 The Author(s) http://creativecommons.org/licenses/by-nc-nd/4.0/ This is an open access article under the CC BY-NC-ND license (http://creativecommons.org/licenses/by-nc-nd/4.0/).
spellingShingle Article
Han, Sang-oh
Ronzitti, Giuseppe
Arnson, Benjamin
Leborgne, Christian
Li, Songtao
Mingozzi, Federico
Koeberl, Dwight
Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction
title Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction
title_full Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction
title_fullStr Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction
title_full_unstemmed Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction
title_short Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction
title_sort low-dose liver-targeted gene therapy for pompe disease enhances therapeutic efficacy of ert via immune tolerance induction
topic Article
url https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6500922/
https://www.ncbi.nlm.nih.gov/pubmed/31073535
http://dx.doi.org/10.1016/j.omtm.2019.04.005
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