Cargando…

Antisense oligonucleotides: A primer

There are few disease-modifying therapeutics for neurodegenerative diseases, but successes on the development of antisense oligonucleotide (ASO) therapeutics for spinal muscular atrophy and Duchenne muscular dystrophy predict a robust future for ASOs in medicine. Indeed, existing pipelines for the d...

Descripción completa

Detalles Bibliográficos
Autores principales: Scoles, Daniel R., Minikel, Eric V., Pulst, Stefan M.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Wolters Kluwer 2019
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6501637/
https://www.ncbi.nlm.nih.gov/pubmed/31119194
http://dx.doi.org/10.1212/NXG.0000000000000323