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Efficacy of pentosan polysulfate in in vitro models of lysosomal storage disorders: Fabry and Gaucher Disease
Gaucher and Fabry diseases are the most prevalent sphingolipidoses. Chronic inflammation is activated in those disorders, which could play a role in pathogenesis. Significant degrees of amelioration occur in patients upon introduction of specific therapies; however, restoration to complete health st...
Autores principales: | Crivaro, Andrea N., Mucci, Juan M., Bondar, Constanza M., Ormazabal, Maximiliano E., Ceci, Romina, Simonaro, Calogera, Rozenfeld, Paula A. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Public Library of Science
2019
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6544267/ https://www.ncbi.nlm.nih.gov/pubmed/31150494 http://dx.doi.org/10.1371/journal.pone.0217780 |
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