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An AAV-SGCG Dose-Response Study in a γ-Sarcoglycanopathy Mouse Model in the Context of Mechanical Stress

Sarcoglycanopathies are rare autosomic limb girdle muscular dystrophies caused by mutations in one of the genes coding for sarcoglycans. Sarcoglycans form a complex, which is an important part of the dystrophin-associated glycoprotein complex and which protects the sarcolemma against muscle contract...

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Detalles Bibliográficos
Autores principales:	Israeli, David, Cosette, Jérémie, Corre, Guillaume, Amor, Fatima, Poupiot, Jérôme, Stockholm, Daniel, Montus, Marie, Gjata, Bernard, Richard, Isabelle
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	American Society of Gene & Cell Therapy 2019
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6545357/ https://www.ncbi.nlm.nih.gov/pubmed/31194043 http://dx.doi.org/10.1016/j.omtm.2019.04.007

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