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Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis
Autores principales: | , , , , , , , , , , , , , , , , , , , , , , , , |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
John Wiley and Sons Inc.
2018
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6588006/ https://www.ncbi.nlm.nih.gov/pubmed/30014500 http://dx.doi.org/10.1002/hep.30160 |
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author | Tucci, Francesca Calbi, Valeria Barzaghi, Federica Migliavacca, Maddalena Ferrua, Francesca Bernardo, Maria Ester Canarutto, Daniele Consiglieri, Giulia Recupero, Salvatore Calzatini, Francesco Gabaldo, Michela Lucano, Caterina Casiraghi, Miriam Darin, Silvia Dionisio, Francesca Marktel, Sarah Cestone, Enza Finazzi, Renato Mieli‐Vergani, Giorgina Boeri, Enzo Appleby, Jonathan Abd Elaziz, Dalia Ciceri, Fabio Aiuti, Alessandro Cicalese, Maria Pia |
author_facet | Tucci, Francesca Calbi, Valeria Barzaghi, Federica Migliavacca, Maddalena Ferrua, Francesca Bernardo, Maria Ester Canarutto, Daniele Consiglieri, Giulia Recupero, Salvatore Calzatini, Francesco Gabaldo, Michela Lucano, Caterina Casiraghi, Miriam Darin, Silvia Dionisio, Francesca Marktel, Sarah Cestone, Enza Finazzi, Renato Mieli‐Vergani, Giorgina Boeri, Enzo Appleby, Jonathan Abd Elaziz, Dalia Ciceri, Fabio Aiuti, Alessandro Cicalese, Maria Pia |
author_sort | Tucci, Francesca |
collection | PubMed |
description | |
format | Online Article Text |
id | pubmed-6588006 |
institution | National Center for Biotechnology Information |
language | English |
publishDate | 2018 |
publisher | John Wiley and Sons Inc. |
record_format | MEDLINE/PubMed |
spelling | pubmed-65880062019-07-02 Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis Tucci, Francesca Calbi, Valeria Barzaghi, Federica Migliavacca, Maddalena Ferrua, Francesca Bernardo, Maria Ester Canarutto, Daniele Consiglieri, Giulia Recupero, Salvatore Calzatini, Francesco Gabaldo, Michela Lucano, Caterina Casiraghi, Miriam Darin, Silvia Dionisio, Francesca Marktel, Sarah Cestone, Enza Finazzi, Renato Mieli‐Vergani, Giorgina Boeri, Enzo Appleby, Jonathan Abd Elaziz, Dalia Ciceri, Fabio Aiuti, Alessandro Cicalese, Maria Pia Hepatology Clinical Observations in Hepatology John Wiley and Sons Inc. 2018-11-13 2018-12 /pmc/articles/PMC6588006/ /pubmed/30014500 http://dx.doi.org/10.1002/hep.30160 Text en © 2018 The Authors. Hepatology published by Wiley Periodicals, Inc. on behalf of American Association for the Study of Liver Diseases. This is an open access article under the terms of the http://creativecommons.org/licenses/by-nc/4.0/ License, which permits use, distribution and reproduction in any medium, provided the original work is properly cited and is not used for commercial purposes. |
spellingShingle | Clinical Observations in Hepatology Tucci, Francesca Calbi, Valeria Barzaghi, Federica Migliavacca, Maddalena Ferrua, Francesca Bernardo, Maria Ester Canarutto, Daniele Consiglieri, Giulia Recupero, Salvatore Calzatini, Francesco Gabaldo, Michela Lucano, Caterina Casiraghi, Miriam Darin, Silvia Dionisio, Francesca Marktel, Sarah Cestone, Enza Finazzi, Renato Mieli‐Vergani, Giorgina Boeri, Enzo Appleby, Jonathan Abd Elaziz, Dalia Ciceri, Fabio Aiuti, Alessandro Cicalese, Maria Pia Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis |
title | Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis |
title_full | Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis |
title_fullStr | Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis |
title_full_unstemmed | Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis |
title_short | Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis |
title_sort | successful treatment with ledipasvir/sofosbuvir in an infant with severe combined immunodeficiency caused by adenosine deaminase deficiency with hcv allowed gene therapy with strimvelis |
topic | Clinical Observations in Hepatology |
url | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6588006/ https://www.ncbi.nlm.nih.gov/pubmed/30014500 http://dx.doi.org/10.1002/hep.30160 |
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