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Brain-enriched microRNAs circulating in plasma as novel biomarkers for Rett syndrome
Rett syndrome (RTT) is a severe neurodevelopmental disorder caused by mutations in the X-linked gene MECP2 (methyl-CpG-binding protein 2). Minimally invasive and accurate biomarkers of disease progression and treatment response could facilitate screening of therapeutic compounds in animal models, en...
Autores principales: | Sheinerman, Kira, Djukic, Aleksandra, Tsivinsky, Vladimir G., Umansky, Samuil R. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Public Library of Science
2019
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6619658/ https://www.ncbi.nlm.nih.gov/pubmed/31291284 http://dx.doi.org/10.1371/journal.pone.0218623 |
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