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Danazol: An Effective and Underutilised Treatment Option in Diamond-Blackfan Anaemia

Diamond-Blackfan anaemia (DBA) is a rare congenital red cell aplasia that presents in infancy. The exact molecular mechanism of ineffective erythropoiesis and red cell aplasia remains unclear, rendering targeted therapy elusive. The mainstay treatment of DBA is with regular blood transfusion and lon...

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Detalles Bibliográficos
Autores principales:	Chai, Kern Y., Quijano, Cara J., Chiruka, Shingirai
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Hindawi 2019
Materias:	Case Report
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6636591/ https://www.ncbi.nlm.nih.gov/pubmed/31355022 http://dx.doi.org/10.1155/2019/4684156

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