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Forced vital capacity and cross-domain late-onset Pompe disease outcomes: an individual patient-level data meta-analysis
BACKGROUND: Late-onset Pompe disease (LOPD) is a rare, metabolic disease primarily affecting the musculoskeletal and respiratory systems. Forced vital capacity (FVC) is commonly used to measure pulmonary function; however, associations between FVC and other LOPD outcomes remain unclear. METHODS: A s...
Autores principales: | Berger, Kenneth I., Kanters, Steve, Jansen, Jeroen P., Stewart, Andrew, Sparks, Susan, Haack, Kristina An, Bolzani, Anna, Siliman, Gaye, Hamed, Alaa |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Springer Berlin Heidelberg
2019
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6687674/ https://www.ncbi.nlm.nih.gov/pubmed/31187190 http://dx.doi.org/10.1007/s00415-019-09401-1 |
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