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Patient-reported outcomes in patients with cystic fibrosis with a G551D mutation on ivacaftor treatment: results from a cross-sectional study

BACKGROUND: Clinical studies demonstrate that ivacaftor (IVA) improves health-related quality of life (HRQoL) in patients aged ≥6 years with cystic fibrosis (CF). The real-world impact of IVA and standard of care (SOC) in groups of patients with G551D and F508del mutations, respectively, was assesse...

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Detalles Bibliográficos
Autores principales:	Bell, Scott C., Mainz, Jochen G., MacGregor, Gordon, Madge, Susan, Macey, Julie, Fridman, Moshe, Suthoff, Ellison D., Narayanan, Siva, Kinnman, Nils
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2019
Materias:	Research Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6693259/ https://www.ncbi.nlm.nih.gov/pubmed/31409396 http://dx.doi.org/10.1186/s12890-019-0887-6

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