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A Muscle Hybrid Promoter as a Novel Tool for Gene Therapy
Gene therapy is a promising strategy to cure rare diseases. The lack of regulatory sequences ensuring specific and robust expression in skeletal and cardiac muscle is a substantial limitation of gene therapy efficiency targeting the muscle tissue. Here we describe a novel muscle hybrid (MH) promoter...
Autores principales: | Piekarowicz, Katarzyna, Bertrand, Anne T., Azibani, Feriel, Beuvin, Maud, Julien, Laura, Machowska, Magdalena, Bonne, Gisèle, Rzepecki, Ryszard |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
American Society of Gene & Cell Therapy
2019
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6807297/ https://www.ncbi.nlm.nih.gov/pubmed/31660418 http://dx.doi.org/10.1016/j.omtm.2019.09.001 |
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