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Real-World Outcomes with Lomitapide Use in Paediatric Patients with Homozygous Familial Hypercholesterolaemia

INTRODUCTION: Homozygous familial hypercholesterolaemia (HoFH) is a rare, autosomal disease affecting the clearance of low-density lipoprotein cholesterol (LDL-C) from circulation, and leading to early-onset atherosclerotic cardiovascular disease (ASCVD). Treatment consists mainly of statins, lipopr...

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Detalles Bibliográficos
Autores principales:	Ben-Omran, Tawfeg, Masana, Luis, Kolovou, Genovefa, Ariceta, Gema, Nóvoa, F. Javier, Lund, Allan M., Bogsrud, Martin P., Araujo, María, Hussein, Osamah, Ibarretxe, Daiana, Sanchez-Hernández, Rosa M., Santos, Raul D.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer Healthcare 2019
Materias:	Case Series
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6824397/ https://www.ncbi.nlm.nih.gov/pubmed/31102204 http://dx.doi.org/10.1007/s12325-019-00985-8

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