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Molecular Therapies for Choroideremia
Advances in molecular research have culminated in the development of novel gene-based therapies for inherited retinal diseases. We have recently witnessed several groundbreaking clinical studies that ultimately led to approval of Luxturna, the first gene therapy for an inherited retinal disease. In...
Autores principales: | Cehajic Kapetanovic, Jasmina, Barnard, Alun R., MacLaren, Robert E. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2019
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6826983/ https://www.ncbi.nlm.nih.gov/pubmed/31548516 http://dx.doi.org/10.3390/genes10100738 |
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