Cargando…
Curing Hemoglobinopathies: Challenges and Advances of Conventional and New Gene Therapy Approaches
Inherited hemoglobin disorders, including beta-thalassemia (BT) and sickle-cell disease (SCD), are the most common monogenic diseases worldwide, with a global carrier frequency of over 5%.1 With migration, they are becoming more common worldwide, making their management and care an increasing concer...
| Autores principales: | , , , |
|---|---|
| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
Università Cattolica del Sacro Cuore
2019
|
| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6827604/ https://www.ncbi.nlm.nih.gov/pubmed/31700592 http://dx.doi.org/10.4084/MJHID.2019.067 |