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A Systematic Review of the Health Economics of Pompe Disease
BACKGROUND: Pompe disease is a rare, severe neuromuscular disease with high mortality and substantial clinical and humanistic burden. However, the economic burden of Pompe disease and the health economic value of its treatments are not well understood. The objectives of this systematic review were t...
Autores principales: | Schoser, Benedikt, Hahn, Andreas, James, Emma, Gupta, Digant, Gitlin, Matthew, Prasad, Suyash |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Springer International Publishing
2019
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6861413/ https://www.ncbi.nlm.nih.gov/pubmed/31049836 http://dx.doi.org/10.1007/s41669-019-0142-3 |
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