Tamoxifen in Duchenne muscular dystrophy (TAMDMD): study protocol for a multicenter, randomized, placebo-controlled, double-blind phase 3 trial

BACKGROUND: Duchenne muscular dystrophy (DMD) is an inherited neuromuscular disorder of childhood with a devastating disease course. Several targeted gene therapies and molecular approaches have been or are currently being tested in clinical trials; however, a causative therapy is still not availabl...

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Detalles Bibliográficos
Autores principales: Nagy, Sara, Hafner, Patricia, Schmidt, Simone, Rubino-Nacht, Daniela, Schädelin, Sabine, Bieri, Oliver, Fischer, Dirk
Formato: Online Artículo Texto
Lenguaje:English
Publicado: BioMed Central 2019
Materias:
Study Protocol
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6869203/
https://www.ncbi.nlm.nih.gov/pubmed/31752977
http://dx.doi.org/10.1186/s13063-019-3740-6

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