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Teaching an Old Molecule New Tricks: Drug Repositioning for Duchenne Muscular Dystrophy
Duchenne muscular dystrophy (DMD) is one of the most severe forms of inherited muscular dystrophies. The disease is caused by the lack of dystrophin, a structurally essential protein; hence, a definitive cure would necessarily have to pass through some form of gene and/or cell therapy. Cell- and gen...
| Autores principales: | , , , , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
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MDPI
2019
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| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6929176/ https://www.ncbi.nlm.nih.gov/pubmed/31801292 http://dx.doi.org/10.3390/ijms20236053 |