Cargando…
Funding community collaboration to develop effective therapies for neurofibromatosis type 1 tumors
The time from identifying a drug target to a new drug approval is often measured in decades and can take even longer for therapies to treat rare diseases. In fact, 95% of rare diseases do not have a specific therapy approved at all. Coordinated efforts to augment the drug development pipeline along...
Autores principales: | La Rosa, Salvatore, Browder, Vidya, Bakker, Annette C, Blakeley, Jaishri O, Verma, Sharad K, Wong, Ling M, Morris, Jill, Bora, Naba |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
John Wiley and Sons Inc.
2019
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6949486/ https://www.ncbi.nlm.nih.gov/pubmed/31793149 http://dx.doi.org/10.15252/emmm.201911656 |
Ejemplares similares
-
Engaging a community to enable disease-centric data sharing with the NF Data Portal
por: Allaway, Robert J., et al.
Publicado: (2019) -
COVID-19 in people with neurofibromatosis 1, neurofibromatosis 2, or schwannomatosis
por: Banerjee, Jineta, et al.
Publicado: (2023) -
Neurofibromatosis Type 1–Associated MPNST State of the Science: Outlining a Research Agenda for the Future
por: Reilly, Karlyne M., et al.
Publicado: (2017) -
Rethinking the nonprofit foundation: an emerging niche in the rare disease ecosystem
por: Bakker, Annette C, et al.
Publicado: (2017) -
A qualitative study of the impact of plexiform neurofibromas on need fulfilment in adults with neurofibromatosis type 1
por: Heaney, Alice, et al.
Publicado: (2019)