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Case-control study about the acceptance of Pegvaliase in Phenylketonuria

INTRODUCTION: Pegvaliase is a novel enzyme substitution therapy approved by the European Drug Administration (EDA) in May 2019 for the treatment of Phenylketonuria (PKU) in adults and children ≥16 years of age. The pegylated phenylalanine ammonia lyase is isolated from bacteria and therefore provoke...

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Detalles Bibliográficos
Autor principal: Krämer, Johannes
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Elsevier 2020
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6957785/
https://www.ncbi.nlm.nih.gov/pubmed/31956507
http://dx.doi.org/10.1016/j.ymgmr.2019.100557