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Safety Study of Sodium Pentosan Polysulfate for Adult Patients with Mucopolysaccharidosis Type II

Current therapies for the mucopolysaccharidoses (MPS) do not effectively address skeletal and neurological manifestations. Pentosan polysulfate (PPS) is an alternative treatment strategy that has been shown to improve bone architecture, mobility, and neuroinflammation in MPS animals. The aims of thi...

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Detalles Bibliográficos
Autores principales:	Orii, Kenji, Lim, Alaena, Tomatsu, Shunji, Stapleton, Molly, Suzuki, Yasuyuki, Simonaro, Calogera M., Schuchman, Edward H., Fukao, Toshiyuki, Matsumoto, Tadashi
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2019
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6963688/ https://www.ncbi.nlm.nih.gov/pubmed/31861164 http://dx.doi.org/10.3390/diagnostics9040226

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