Novel Enzyme Replacement Therapies for Neuropathic Mucopolysaccharidoses

Although the advent of enzyme replacement therapy (ERT) for mucopolysaccharidoses (MPS) has paved the way for the treatment for these hereditary disorders, the blood brain barrier (BBB) has prevented patients with MPS involving the central nervous system (CNS) from benefitting from ERT. Therefore, f...

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Detalles Bibliográficos
Autores principales: Sato, Yuji, Okuyama, Torayuki
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2020
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7014430/
https://www.ncbi.nlm.nih.gov/pubmed/31936354
http://dx.doi.org/10.3390/ijms21020400

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7014430/
https://www.ncbi.nlm.nih.gov/pubmed/31936354
http://dx.doi.org/10.3390/ijms21020400

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