Cargando…
Novel Enzyme Replacement Therapies for Neuropathic Mucopolysaccharidoses
Although the advent of enzyme replacement therapy (ERT) for mucopolysaccharidoses (MPS) has paved the way for the treatment for these hereditary disorders, the blood brain barrier (BBB) has prevented patients with MPS involving the central nervous system (CNS) from benefitting from ERT. Therefore, f...
| Autores principales: | , |
|---|---|
| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
MDPI
2020
|
| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC7014430/ https://www.ncbi.nlm.nih.gov/pubmed/31936354 http://dx.doi.org/10.3390/ijms21020400 |